The Needs of the Few
Date
2018-12
Authors
Smith, Alexander
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Abstract
Description
An essay on the story of Mila, a 7 year old girl affected by Batten disease, an extremely rare neurodegenerative genetic disorder. Using Mila’s case as an example, this essay explores recent strides made in personalized medicine and antisense oligonucleotide drug therapy used to treat rare genetic diseases, along with discussion of ethical, legal, and social issues stemming from this topic.
Keywords
Batten disease